NACFC 2022 | S01: Design of Clinical Trials to Evaluate Nucleotide-Based Interventions

The purpose of this symposium is to provide up-to-date information on active and upcoming genetic therapy trials in persons with cystic fibrosis. This will review the important considerations in study design, conduct, and outcomes measures of the growing field of nucleotide-based treatments.

Originally recorded November 3, 2022.