How AAV Gene Transfer Works - General Audience

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This brief animation, designed for a general audience, illustrates the basics of AAV gene transfer technology.
  1. uniQure
  2. AAV
  3. gene transfer
  4. gene therapy
  5. uniQure
  6. MOA
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Комментарии
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the animations here are insane! Thank you, very useful to see the whole process animated like this, very educational. helps understand.

shayanghafary
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Exceptional animations. Amazing how seeing it like this really settles in the feeling of just how incredible this technology is to manipulate our already unbelievable physiological mechanisms

XxSolvexX
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Magnificent video. Thank you UniQure!!

juanpabloparzela
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thats the beauty of molecular biology...i am in love ...😍😍

chittaranjanpal
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Does anyone know what company produced this animation?!

jacklynallen
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it forms episome like a second DNA not integrated cells own DNA if there is a missing gene it may work but if cells own DNA produce faulty protein or wrong protein it is going to build up in body episome will create right protein and at he same time cell's own dna will create wrong protein both

life_
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Excellent video .... !!!! If m-RNA is formed from the transcription of the DNA episome ... what will happen when the cells that have the episomes die ...? .... Do we have to re-inject the patient ...? ... But you will need a different adenovirus ... because for the first one ... the body will have a strong immune response to it ... Maybe a retrovirus ... will solve the problem ...

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