Limb-Girdle Muscular Dystrophy and Gene Therapy

One muscular dystrophy sub-group is called limb-girdle muscular dystrophy, or LGMD. These diseases weaken the muscles of a person’s shoulders, upper arms, hips and thighs. Each subtype of LGMD is caused by a different inherited faulty gene.

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[Ummm-lp]

I have also had muscular dystrophy for 11 years, and now I can’t even get up from a chair or use the bathroom on my own.
And now it's getting much worse.
Because of this, I have become very lonely and now I suffer from severe depression and anxiety.

[ofentsemaboka]

I was born with Limb Girdle Muscular Dystrophy in South Africa, I can't walk properly, I struggle to walk fast, I can't run, I can't jump, I have to balance myself with something in order to stand up, and I struggle to climb up steps..I am 30years, I really wish I can get help of funds to get a the best treatment to slow down the progress of this disease..It started to be more bad in my 20th years..Please help me guys, I really will be happy for those who are willing to help me..

[rb]

I was diagnosed 11 years ago after experiencing symptoms my whole life. The last 5 years it's gotten really bad.

[AlexLeeModernNinja]

Im a 47 year old 100% disabled veteran, who got diagnosed with LGMD type 2D. Was diagnosed approximately 17 years ago, adult onset. I used to walk with a cane for mobility. Currently using Canadian crutches and a power chair for longer distances. I currently do stretches & physical therapy to stay mobile. Swimming also helps. I want to stay active for as long as I can.

Have there been any new programs for gene & cell therapy available or stem cell treatment? How long does a person live with this disease? I was told for adult onset people can live as long as a normal lifespan.

[DM-]

I find a high protein diet along with light exercise really helps. Dont excercise till your muscles cramp or get sore...but exercise keeps the muscles strong. Watch your weight but dont get too thin ....more weight = more effort to move. Its a losing battle but try keep mobile and safe as long as you can

[LadySamurai]

I’ve been diagnosed with LGMD since i was a small kid. I could walk but not run fast and i am very skinny and can’t gain weight.
Around age 13 my neck muscles became weaker and weaker that made me lean with my elbows on my knees when sitting i grew into this position and around 16 maybe 17 my back and neck grew in that position. I can’t sit up straight cause my neck muscles aren’t strong enough so my neck will fall backwards. My muscles are getting weaker and weaker and sadly i am not able to pull up my pants.
But i’m not complaining cause when read messages from other people with LGMD that look less disabled then me have way more issues then me like a lot of pain etc.
I just have pain in my left leg when i sit in my Electric Wheelchair that’s all.
I can still shower myself.
And i make a lot of jokes about my disability like for example that i can walk but i’m just to lazy or that i always train every year for the Marathon.
It’s fun to make jokes about my disability lol

[mamashoni]

This is great! My cousin is working on this!

[luzquinatoa]

My 4 year old nephew juys got diagnosed with it. Very few onset symptoms for now but what can we do to help him. We live in NYC in the United States. He has 1F kind which is a pretty rare form

[nirajshukla]

Any further progress on this therapy and treatment ?, please share

[rajpriya]

when available gene therapy for limb girdle muscular dystrophy

[StampOutTheStigma]

I lost an uncle and my father to LGMD. Have any of these been treatments been tried? Are there clinical trials? How would one become eligible for the gene therapy if they were interested?

[LifeGuru]

Is there any tested treatment for lgmd?

[أبوالعلاء-سش]

svp quelle analyse peut on faire pour connaitre le type de lgmd?

[kamransheikh]

My mother and my maternal uncle is suffering with this disease.
My mother is suffering last 27 years
And uncle last 17 years
They effected at age of 30
If any one having idea kindly contact me please and even I can also share my experience to you also

[rahulsharmapandit]

will gene therapy be the cure of lgmd or it only slow the progression of it

[puttapavani]

Where can I get this treatment is it available in india pl help me

[smithabs]

Am suffering from 6year in the disease of the limb girdle muscular dystrophy 2I treatment plz help me plz cureable treatment plz

[MrBelal]

My uncle suffering LGMD Musculler problem last 20years.

I need Help

[mastermind]

Use homeopathic medicines of lead/plumbum compounds' dilutions & ashwagandha(indian ginseng) in homeopathic mother tincture form for these type of problems.