Gene Therapy in Neuroscience 101

Featuring:
Connie Cepko
Bullard Professor of Genetics and Neuroscience, Harvard Medical School
Professor of Ophthalmology, Massachusetts Eye and Ear Infirmary
Howard Hughes Medical Institute Investigator

David Liu
Thomas Dudley Cabot Professor of the Natural Sciences, Harvard University;
Howard Hughes Medical Institute Investigator

Dr. Cepko discusses the goals of gene therapy, the types of viruses that have vectorized and been used, and why they are being used. Dr. Liu reviews current human gene editing methods and developments. Both highlight examples from their own research.