Duchenne Muscular Dystrophy and Gene Therapy

The most common form of muscular dystrophy is called Duchenne. The disease is caused by a faulty gene that interferes with how muscle cells produce a protein called dystrophin. It’s part of a vital protein complex that works to strengthen and protect muscle fibers.

The subtitling of these videos was funded in part by a donation from Pfizer, Inc.

[SchoolSchoolSchoolSchoolSchool]

this video gave me muscular dis trophy

[shekharreddy]

Any cure for tis disease? If anyone knows please please let ne know.thank you

[LC-spox]

Clinical trials going on right now with pfizer and sarepta!

[natialon]

So if we have girl embryo that is know as a carrier of DMD, could we return this embryo without the fear she will be developing same symptoms as a boy that sick with Duchenne?

[jalalshahshah]

Gene therapy is started any where in world?

[Priyuge]

When we expect muscular dystrophy treatment

[Aaradhyghadge]

Please save my 7year child dmd patient please save my child 😔🙏no money treatment