New promise for gene therapy

The genes we inherit from our forebears help shape our lives - and in too many cases, can cut young lives short well before their time. Now a cutting-edge stem cell therapy is achieving some success, but is still not available in the United States. Martha Teichner reports on a promising new treatment for late infantile metachromatic leukodystrophy.

[Bobomwahaahwahahahahah]

you guys need more sympathy, having a big family is amazing and loving. I am her oldest sister although now I am 13 on this day we r filming for Boston children's hospital please no rood comments only love

[marlacehughes]

My son died of MLD. Absolutely heartbreaking.

[exoticcarsofamerica]

My brother has been diagnosed with white matter leukodystrophy. He is 19 years old. Is there any treatment available to cure these diseases and help my brother stand on his feet?

[swapnauppu]

Hey hi
My Son is 2 years 3 mnths recently diagnosed with MLD.
Showing some symptoms as well.
Please let us know about the treatment and cure🙏

[charmedlilsis]

This is all very inspiring and sad but I can't help but wonder why they chose to keep having children after finding out that any subsequent children they had could have MLD. They have like 4 kids who are younger than the little girl who died. Why keep having kids and taking the chance that they will be born with the disease that already took one of your children?

[michaelermcgowaniv]

Amazing that the HIV virus can be used to help.

[arfakhatoon]

Late infantile metacromatic leucodystrophy treatment are available ?

[marlacehughes]

It's all about the blood brain barrier. That is the challenge.

[guspolly]

I'm not crying, you're crying

[corriscaro]

What an insensitive, cruel thing to say about someone with MLD.

[gallagherscott]

goto canada! they're researching my gene over there!

[SpiralBreeze]

I have no sympathy for anyone addicted to Calliou.