2023 WMIF | Disruptive Dozen #4

New therapies for ALS

Two new treatments were recently approved for ALS, bringing the total number of approved drugs to just seven. One involves a pair of drugs that work together in combination to prevent neurons from dying. The other is a gene-based therapy tailored to patients with a rare genetic form of ALS. While the unmet need for ALS therapies remains high, these new therapies signal an important step forward.