Unmet needs in hemoglobinopathy care

Anna Sureda, MD, PhD, Catalan Institute of Oncology, Duran I Reynals Hospital, Barcelona, Spain, highlights the unmet needs in hemoglobinopathy care in several areas. A standardized referral pathway and the establishment of a multidisciplinary team are necessary for a more focused treatment. In addition, transplantation is a curative approach, and, in the case of transfusion-dependent beta thalassemia and sickle cell disease (SCD), patients do not experience graft-versus host disease (GvHD). New data show reduction of allogeneic hematopoietic stem cell transplantation (alloHSCT)-associated neurotoxicity with the use of novel therapies. This interview took place at the 48th Annual Meeting of the European Group for Blood and Marrow Transplantation (EBMT) 2022, which was held virtually.