World's most expensive medicine treats infants with genetic disorder - BBC News

A baby boy has become one of the first patients to be treated on the UK's NHS with Zolgensma, the world's most expensive medicine.

Little Arthur is one of around 40 children are born with the most severe form of Spinal Muscular Atrophy (SMA) every year.

The gene therapy has a list price of about $2.5m and is manufactured by Novartis Gene Therapies.

#BBCNews

[DD-lyog]

its heart breaking to see a baby in pain😭

[flightgeekyuta]

Jesus, imagine being able to afford this with US health care...

[PLuMUK]

I'm in the UK and I think that this is worth every penny spent by the NHS. Well done to all involved, and blessings to a delightful baby, may your life be as long as possible.

[mansooralli]

Arthur my boy get well soon, We all want to see you running. All my prayers with you son.

[wjf]

My niece died of SMA. This is a miracle drug to every parents nightmare. We also need more widespread screening for this condition.

[cazw]

Bless little Arthur - such a gorgeous boy. Hope his improvement continues 🙏

[elliotelephants]

I’m so glad that this life saving medication is available in the UK now! I’ve seen kids here in the states who have had this medication and it’s genuinely like a miracle 🤍

[richardolivia]

The drug is amazing and needed. The price per dose is disgusting, especially since the companies factor in something beyond Research and Development costs, called “value to patients” when coming up with the final price.The companies basically say “ this is the drug that will give you extended life…now pay us what we think your extended life is worth.” Here in the US we have to pay the co-insurance or completely out of pocket for these extremely expensive drugs, and I don’t know anyone with $2.2 Million to pay for one dose of medicine!

[killertortoise]

Thank god for the NHS, the future of gene therapy is so exciting, I hope more children can benefit from this.

[Ryan-rjmi]

This is a huge news for future gene therapy treatments and cures. I have CMT 2A and I've been patiently waiting for 15 years for something to come out and seeing this brings a smile to my face especially for the people who are suffering from serious types of Muscle Dystrophy and CMT. KEEP THE GOOD NEWS COMING, THERE IS FINNALY HOPE

[niara]

Unfortunately, not everyone can afford this miracle medicine🥺🥺

[moizahadsaggu]

Price is nothing to bring smile to this adorable baby

[khyberkhan]

I am happy to see that the baby is on his way to recovery. Feel sorry for my nephew who is suffering from the same disease, unfortunately we can't afford such expensive treatment.

[amrayousaf]

Nothing is more precious than a child's life and health ..I have lots of love and prayers for this child .live a good and healthy life .

[londonw]

Get well little one. One day there will be cure for eveything. Believe in science, medical research n Intellect only.

[heilmetropolis]

God please bless the baby and those trying to help him...

[csy]

The medicine is ridiculously priced. But it saves the healthcare community a lifetime of support of 1 person with just 1 dose. And the baby will have a chance to grow up and contribute much more to the community

[celestialstar]

Let's all spend a moment to pray for the suffering baby and everyone with SMA and their family members.

[gentry]

Shame on those that have disliked this video.
Happy for Arthur!

[md.hasanuzzaman]

Best wishes for Arthur and Torah....from a father of SMA type I baby.