Efficacy & Long-term Safety of CRISPR/Cas9-mediated Genome Editing in SOD1-linked Mouse Model of ALS

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Efficacy & Long-term Safety of CRISPR/Cas9-mediated Genome Editing in SOD1-linked Mouse Model of ALS

Han-Xiang Deng, MD, PhD
Research Professor of Neurology
Division of Neuromuscular Disease
Davee Department of Neurology
Northwestern University

9th Annual Les Turner Symposium on ALS and Neurorepair
November 12, 2019
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